Alternatives to Rocket Pharmaceuticals

A global biotechnology company focused on developing and commercializing therapies for rare genetic diseases.

Clinical-stage genetic medicine company developing AAV-mediated treatments for cardiovascular and Alzheimer's diseases.

Biotechnology company developing immuno-neurology therapies for neurodegenerative diseases.

Gene therapy company developing treatments for rare inherited diseases.

A biopharmaceutical company focused on developing novel therapies.

Clinical-stage biopharmaceutical company developing gene therapies for rare genetic diseases.

Biotechnology company developing gene therapies and regenerative medicine for heart disease.

Gene therapy company developing transformative treatments for severe genetic diseases.

Biopharmaceutical company focused on rare genetic diseases of obesity.

Ophthalmic pharmaceutical company developing novel treatments for ocular diseases.

Biopharmaceutical company developing novel therapies for rare and ultra-rare genetic diseases.

A global pharmaceutical and biotechnology corporation developing innovative medicines and vaccines for various therapeutic areas.

Biopharmaceutical company focused on developing RNA-targeted therapies for rare genetic diseases.

RD-Biotech develops innovative solutions for drug discovery and development using advanced biotechnology.

Biopharmaceutical company developing therapies for neurodegenerative diseases, focusing on crossing the blood-brain barrier.

Vaxart is a clinical-stage biotechnology company developing oral vaccines for infectious diseases.

Omega Therapeutics is developing a new class of programmable medicines called Epigenomic Controllers.

A biotechnology company developing gene therapy treatments for rare, debilitating genetic diseases.

Moderna is a biotechnology company pioneering mRNA medicine, best known for its COVID-19 vaccine and a broad pipeline of mRNA-based therapeutics.