Alternatives to Spark Therapeutics

Developing genetic medicines and cell therapies for severe diseases using proprietary CRISPR OMNI technology.

Gene therapy company developing treatments for rare inherited diseases.

Developing innovative gene therapies to preserve or restore vision in patients with retinal diseases.

OMGene is a biotechnology company focused on developing gene therapies for rare genetic diseases.

Moderna is a biotechnology company pioneering mRNA medicine, best known for its COVID-19 vaccine and a broad pipeline of mRNA-based therapeutics.

Epicrispr Biotechnologies is a biotechnology company developing novel epigenetic therapies, with a lead program targeting Facioscapulohumeral Muscular Dystrophy (FSHD).

Clinical-stage biotechnology company advancing molecular glue degrader (MGD) medicines.

A life sciences company that has developed a high-throughput platform for mapping molecular cell architecture at nanoscale resolution.

Developing first-and best-in-class antibody-drug conjugates (ADCs) for cancers with high unmet medical need.

Developing human-derived antibodies for inflammatory diseases and cancer using AI and proprietary platforms.

Clinical-stage biopharmaceutical company leveraging a proprietary platform to discover and develop novel precision medicines from fungi.

Clinical-stage biopharmaceutical company developing microbiome-derived immunotherapies for cancer and immune diseases.

A vertically-integrated procurement platform for the life sciences industry.

Leveraging AI and a massive patient tissue dataset to accelerate drug discovery and advance precision medicine.

A clinical-stage biotechnology company developing inobrodib as a first-in-class, oral p300/CBP inhibitor for the treatment of multiple myeloma.

A global leader in clinical pharmacology and bioanalytical sciences.

Biopharmaceutical company developing novel small-molecule therapeutics for rare kidney diseases, particularly Autosomal Dominant Polycystic Kidney Disease (ADPKD).

Freenome is a biotechnology company developing a multi-cancer early detection blood test using machine learning and biology.

Developing novel immunotherapies and diagnostics for cancer.

A biotechnology company developing genetic therapies for rare disorders.