Alternatives to Spark Therapeutics

Ridge Bio is developing a novel gene therapy platform for treating rare genetic diseases.

Biotechnology company developing next-generation gene therapies using a proprietary protein splicing platform.

Developing genetic medicines and cell therapies for severe diseases using proprietary CRISPR OMNI technology.

Gene therapy company developing treatments for rare inherited diseases.

Developing innovative gene therapies to preserve or restore vision in patients with retinal diseases.

A clinical-stage oncology company developing DNA interference (DNAi) based cancer therapies.

OMGene is a biotechnology company focused on developing gene therapies for rare genetic diseases.

Cell and gene therapy company developing biological vehicles for CNS delivery.

Moderna is a biotechnology company pioneering mRNA medicine, best known for its COVID-19 vaccine and a broad pipeline of mRNA-based therapeutics.

A life sciences company that has developed a high-throughput platform for mapping molecular cell architecture at nanoscale resolution.

Clinical-stage biotechnology company advancing molecular glue degrader (MGD) medicines.

Epicrispr Biotechnologies is a biotechnology company developing novel epigenetic therapies, with a lead program targeting Facioscapulohumeral Muscular Dystrophy (FSHD).

A clinical-stage biotechnology company developing inobrodib as a first-in-class, oral p300/CBP inhibitor for the treatment of multiple myeloma.

Leveraging AI and a massive patient tissue dataset to accelerate drug discovery and advance precision medicine.

Clinical-stage biopharmaceutical company developing microbiome-derived immunotherapies for cancer and immune diseases.

A vertically-integrated procurement platform for the life sciences industry.

Developing first-and best-in-class antibody-drug conjugates (ADCs) for cancers with high unmet medical need.

Clinical-stage biopharmaceutical company leveraging a proprietary platform to discover and develop novel precision medicines from fungi.

Developing human-derived antibodies for inflammatory diseases and cancer using AI and proprietary platforms.

A global leader in clinical pharmacology and bioanalytical sciences.